US FDA Grants Expanded Approval of ELEVIDYS Gene Therapy for DMD Patients Ages 4 and Above

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Marathon Pharmaceuticals Presents Analyses at AAN of a Phase III Clinical Study of Deflazacort in Patients with Duchenne Muscular Dystrophy (DMD)

Investigational Drug Deflazacort Has Fast Track Status, Orphan Drug Designation and Rare Pediatric Disease Designation for DMD from FDA