US FDA Grants Expanded Approval of ELEVIDYS Gene Therapy for DMD Patients Ages 4 and Above

Innovations in Care

We provide programs and services that transform the lives of people affected by neuromuscular disease.

On-Demand Webinars

The Development Journey of Spinraza® (nusinersen): From Advocacy to Treatment and Beyond
The Development Journey of Spinraza® (nusinersen): From Advocacy to Treatment and Beyond
Community Industry Update Webinars
Jan 27, 2022
Harmony Investigates Excessive Daytime Sleepiness, Non Muscular Symptoms in Myotonic Dystrophy
Harmony Investigates Excessive Daytime Sleepiness, Non Muscular Symptoms in Myotonic Dystrophy
Community Industry Update Webinars
Supported by: Harmony Biosciences
Dec 8, 2021
Adult Neuromuscular Seminar
Adult Neuromuscular Seminar
MDA Engage Community Education Seminars
Supported by: Genentech
Dec 4, 2021
Spinal Muscular Atrophy (SMA) Symposium
Spinal Muscular Atrophy (SMA) Symposium
MDA Engage Symposia
Supported by: Biogen, Genentech
Nov 13, 2021
Pediatric Neuromuscular Disease Care
Pediatric Neuromuscular Disease Care
MDA Engage Community Education Seminars
Supported by: Amicus Therapeutics
Oct 23, 2021
Facioscapulohumeral Muscular Dystrophy (FSHD)
Facioscapulohumeral Muscular Dystrophy (FSHD)
MDA Engage Community Webinars
Presenters: Johanna Hamel, neurologist at the University of Rochester
Supported by: Fulcrum Therapeutics
Oct 21, 2021
MDA Engage: Facioscapulohumeral Muscular Dystrophy (FSHD)
MDA Engage: Facioscapulohumeral Muscular Dystrophy (FSHD)
MDA Engage Community Webinars
Supported by: Fulcrum Therapeutics
Oct 21, 2021
Mental Health
Mental Health
Facebook Live
Supported by: Amylyx, Genentech, Mitsubishi Tanabe Pharma America
Oct 21, 2021
Newborn Screening
Newborn Screening
MDA Engage Community Webinars
Presenters: Dr. Marcia Felker from Indiana University Health-Riley Children’s Hospital
Supported by: Astellas, Sanofi Genzyme
Oct 6, 2021
Caregiver Seminar
Caregiver Seminar
MDA Engage Community Education Seminars
Supported by: Mitsubishi Tanabe Pharma America
Sep 25, 2021
2021 Engage Myasthenia Gravis Symposium
2021 Engage Myasthenia Gravis Symposium
MDA Engage Symposia
Supported by: Alexion, Argenx, AstraZeneca Rare Disease, Horizon Therapeutics, UCB
Sep 18, 2021
Your Future, Your Family and Neuromuscular Disease
Your Future, Your Family and Neuromuscular Disease
MDA Engage Community Webinars
Presenters: Jordan Bontrager, Genetic Counselor from the University of Rochester Medical Center
Sep 14, 2021
Duchenne Muscular Dystrophy Symposium
Duchenne Muscular Dystrophy Symposium
MDA Engage Symposia
Supported by: Avidity Biosciences, Biomarin, PTC Therapeutics, Sarepta Therapeutics, Solid Biosciences
Aug 14, 2021
Medical Equipment and Assistive Devices for Neuromuscular Disease - Part 2
Medical Equipment and Assistive Devices for Neuromuscular Disease - Part 2
MDA Engage Community Webinars
Presenters: Vicky Kern, Physical Therapist
Aug 10, 2021
2021 MDA Engage Charcot-Marie-Tooth (CMT) Family Panel
2021 MDA Engage Charcot-Marie-Tooth (CMT) Family Panel
MDA Family Panel
Aug 3, 2021
Charcot-Marie-Tooth (CMT)
Charcot-Marie-Tooth (CMT)
MDA Family Panel
Aug 3, 2021
PT, Exercise and Pompe Disease
PT, Exercise and Pompe Disease
MDA Engage Community Webinars
Presenters: Scarlett Morris and Mary Crouch Young, Physical Therapists, from the University of Kansas Medical Center
Supported by: Amicus Therapeutics, AskBio, Astellas, Sanofi Genzyme
Jul 28, 2021
Mental Health and Amyotrophic Lateral Sclerosis (ALS)
Mental Health and Amyotrophic Lateral Sclerosis (ALS)
MDA Engage Community Webinars
Supported by: Amylyx, Biogen, Mitsubishi Tanabe Pharma America
Jul 27, 2021
LEMS and MG: Knowing the Difference and Getting a Diagnosis
LEMS and MG: Knowing the Difference and Getting a Diagnosis
Community Industry Update Webinars
Supported by: Catalyst Pharmaceuticals
Jul 22, 2021
Introduction to the Diagnostic Odyssey of Neuromuscular Disease
Introduction to the Diagnostic Odyssey of Neuromuscular Disease
MDA Engage Community Webinars
Presenters: Mackenzie Blaile, MS, LGC, and Melissa Gibbons, MS, LGC, certified genetic counselors from Children’s Hospital Colorado
Supported by: Pfizer
Jul 15, 2021
Medical Equipment and Assistive Devices for Neuromuscular Disease – Part 1
Medical Equipment and Assistive Devices for Neuromuscular Disease – Part 1
MDA Engage Community Webinars
Presenters: Vicky Kern, Physical Therapists
Supported by: Hillrom
Jul 10, 2021
Polymyositis and Dermatomyositis
Polymyositis and Dermatomyositis
MDA Engage Community Webinars
Presenters: Dr. Namita Goyal, Co-Director of the UC Irvine-MDA ALS and Neuromuscular Center
Supported by: Kezar Life Sciences
Jun 30, 2021
Adaptive Recreation
Adaptive Recreation
Facebook Live
Supported by: Koolway Sports
Jun 30, 2021
Mental Health and Limb-Girdle Muscular Dystrophy
Mental Health and Limb-Girdle Muscular Dystrophy
MDA Engage Community Webinars
Presenters: Monique Costello, Clinical Social Worker from Washington University Neuromuscular Disease Center
Jun 23, 2021
Creating strong connections and relationships
Creating strong connections and relationships
MDA Engage Community Webinars
Presenters: Paige Lembeck, a Pediatric Psychologist and Assistant Clinical Professor at the Yale Child Study Center
Jun 10, 2021