Be a light of hope this holiday season. Ignite more progress, restore more freedom, and inspire more hope for families living with neuromuscular disease.

Innovations in Care

We provide access to support and programs that empower the lives of people living with neuromuscular diseases.

Access Workshop: Access to Gene Therapy


Learning Module

Take the Workshop

This workshop is designed to provide an overview of common considerations for individuals and caregivers regarding access to gene therapy treatment. This workshop will introduce a variety of gene therapy treatments, explain the FDA drug approval process, address insurance coverage options, present common considerations before, during and after treatment, and more.

How To Use the Platform

Coassemble is the platform used for this workshop and you will need to create an account. To assist in setting up your account, please reference this How To Guide. You can access these workshops on Coassemble from any device at any time. Once you have created your account, if you forget your password, click the Forgot Password? link and follow the steps to set up a new one.

Should you experience problems viewing this workshop or have questions, please reach out to access@mdausa.org.