Medical Educational Resource
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Genetic Approaches to DMD Therapy
Activity Snapshot
Activity Type:
PowerPoint
Release Date:
Wednesday, April 28, 2021
Faculty
Russell J. Butterfield, MD, PhD
Associate Professor of Pediatric Neurology
University of Utah Health, Primary Children’s Hospital, and Shriners Hospitals for Children, Salt Lake City, UT Director, Utah Program for Inherited Neuromuscular Disorders
Activity Overview:
This speaker slide set will highlight the need for a working knowledge of genetics in the evolving treatment landscape for Duchenne muscular dystrophy (DMD). The speaker slide set provides an overview of the challenges and unique aspects of the approaches of genetic therapies currently on the market and in development.
Learning Objectives:
- Appreciate the need for a working knowledge of genetics in the evolving treatment landscape for Duchenne muscular dystrophy (DMD)
- Identify the specific challenges of the DMD gene as they relate to development of genetic therapies
- Understand the unique aspects of each approach of genetic therapies on the market and in development
- Effectively counsel patients and their families about available and upcoming genetic therapies for DMD
