In connection with a gene transfer clinical trial, investigators at Nationwide Children's Hospital in Columbus, Ohio, are seeking people with Becker muscular dystrophy (BMD) for participation in a patient registry.
The investigators say the registry will provide information that will:
Follistatin is a protein that promotes muscle growth and strength. In 2009, researchers showed that genes for the follistatin protein increased strength when injected into the leg muscles of monkeys.
The patient registry project — Clinical Outcomes Studies in Becker Muscular Dystrophy (BMD) and Sporadic Inclusion-Body Myositis (sIBM)— involves tests of muscle strength and function. (At this time, the patient registry is seeking only people with BMD, not sporadic inclusion-body myositis.)
Prospective participants in the registry must:
Prospective participants in the registry must not:
Contact Lindsay Alfano in Columbus, Ohio, at (614) 722-6881 or firstname.lastname@example.org.