Quest Magazine

A Landmark Development for the Duchenne MD Community

First Human SMA Gene Transfer Therapy Trial Opens

How Do Neuromuscular Disorders Affect People's Lives?

Tirasemtiv May Slow Respiratory Decline in ALS

SMA: ISIS-SMNRx Shows Benefit in Infants, Children

DMD: Prosensa Pursuing Path Forward for Drisapersen

ALS: Experimental Drug Tirasemtiv Fails To Show Efficacy in Phase 2b Trial

Background:

 

Bret Michaels Fights Back Against Muscle Disease at Exclusive Ride for Life XXVII Performance to Benefit MDA

Shape of Genetic Material Matters in C9ORF72-Related ALS

MDA Thrilled FDA Will Consider Accelerated Approval for New Muscle Disease Drug Aimed at DMD

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