Quest Magazine

Sarepta Announces Revised Timeline for Eteplirsen FDA Application

Boys with Duchenne muscular dystrophy between the ages of seven and 16 are now being recruited to participate in a phase 3 clinical trial to evaluate the effectiveness and safety of eteplirsen in treating DMD.

SMA: Further Data on ISIS-SMNRx Shows Promising Results

Isis Pharmaceuticals, developer of the experimental spinal muscular atrophy (SMA) drug ISIS-SMNRx, revealed positive results from phase 2 clinical studies of the drug focusing on infants and children with SMA. The new data, which was shared on October 10 by ISIS representatives attending the 19th International World Muscle Society Congress in Berlin, included the following highlights:

LEMS: Firdapse Study Shows Encouraging Results

Catalyst Pharmaceuticals, a biopharmaceutical company focused on rare debilitating diseases, announced encouraging results on Sept. 29, 2014, from its phase 3 clinical trial of Firdapse (amifampridine phosphate tablets equivalent to 10mg amifampridine) for the symptomatic treatment of Lambert-Eaton myasthenic syndrome (LEMS).

MDA Team Momentum Fights Back Against Muscle Disease at The 2014 Bank of...

#MDATeamMomentum

CHICAGO, Oct. 2, 2014 — The Muscular Dystrophy Association's new nationwide endurance program MDA Team Momentum will take huge strides in the fight for muscle health at the 2014 Bank of America Chicago Marathon  on Sunday, Oct. 12  to help support MDA's mission to save and improve lives of people fighting muscle disease.

MDA Names Dr. Grace Pavlath to Head Scientific Program as Research Department Intensifies Focus on Ushering Treatments Through Drug Pipeline

National Association of Letter Carriers Raises $1.4 Million to Help Fight Muscle Disease

CHICAGO, Sept. 10, 2014 – The Muscular Dystrophy Association today announced that the National Association of Letter Carriers (NALC) has raised more than $1.4 million over the past year to help save and improve the lives of people fighting muscle disease.

Vital funds provided by NALC long have supported MDA’s world-renowned research efforts, life-changing health care services and community support programs, including MDA summer camp and advocacy efforts that involve local communities.

CITGO Raises $13.6 Million to Help Fight Muscle Disease

CHICAGO,  Sept. 8 2014 – CITGO Petroleum Corporation and its employees and branded Marketers raised more than  $13.6 million over the past year to help the Muscular Dystrophy Association save and improve the lives of people fighting muscle disease. Vital funds provided by CITGO have long supported MDA’s world renowned research efforts, life-changing health care services and community support programs, including MDA summer camp and advocacy efforts that involve local communities. 

IAFF Raises $28 Million To Fight Muscle Disease

CHICAGO, Sept. 4, 2014 – The International Association of Fire Fighters (IAFF) raised more than $28 million over the past year to help the Muscular Dystrophy Association save and improve the lives of people fighting muscle disease.   

Sponsors, Celebrities and Donors Give Generously Through MDA Show of Strength Telethon

CEO Praises Supporters, Pledges Progress
In Fight Against Muscle Disease

 

$52.3 Million and Counting on the MDA Show of Strength Telethon

Donations To Be Tallied through Midnight Monday

 

Watch and Donate on mda.org

 

Pages