Quest Magazine

SMA: Need for SMN-Raising Treatment Highest Very Early in Life

DMD, BMD: Ataluren Did Not Receive Early Approval in Europe

Augie’s Quest To Transition from MDA to the ALS Therapy Development Institute

'Clump-Busting' Molecule Targets Misfolded Proteins in ALS

Sailormen Inc. Popeyes Annual ‘Appetite For A Cure’ Campaign Helps Fight Back Against Muscular Dystrophy

PTC Therapeutics Provides Update On CHMP Opinion For Conditional Approval Of Ataluren For Nonsense Mutation Duchenne Muscular Dystrophy

MMD2: Designer Compounds Free a Trapped Protein

FA: BioMarin To Develop Former Repligen Drugs

Animal Studies Bode Well for MTM Gene Therapy

FA Drug RG2833 Moves from Repligen to BioMarin