BREAKING NEWS: New drug approved by the FDA for Duchenne muscular dystrophy. Learn more about this new treatment option.

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Marathon Pharmaceuticals Presents Analyses at AAN of a Phase III Clinical Study of Deflazacort in Patients with Duchenne Muscular Dystrophy (DMD)

Investigational Drug Deflazacort Has Fast Track Status, Orphan Drug Designation and Rare Pediatric Disease Designation for DMD from FDA